miRNA
miRNA have recently attracted much attention as a potential cure for various diseases based on their ability to suppress the expression of pathologic genes. Curamys has identified a specific miRNA that is a key etiological factor in the pathogenesis of rare diseases including Duchenne muscular dystrophy, Lou Gehrig’s disease (i.e., amyotrophic lateral sclerosis), and nonketotic hyperglycinemia and is devoted to developing therapies leveraging this miRNA.
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